Previously, the McGuire group at NIH reported that children with mitochondrial disease in general experience serious …
Expert Series: Stride Study for PMM Patients
Join MitoAction and Dr. Alex Dorenbaum, Chief Medical Officer at Reneo Pharmaceuticals, as they discuss the Stride Study …
Expert Series: Understanding Upcoming MCADD Trials
There are two new MCADD trials that have started in recent months. One explores the use Dojolvi (triheptanoin) and the …
Expert Series: Ultra-Rare Mitochondrial Diseases: Development Challenges and Opportunities
Join CEO of Stealth Biotherapeutics Reenie McCarthy, and special guest Shelley Bowen, Director of Family Services and …
Expert Series: Modeling mitochondrial diseases with patient-derived stem cells and brain organoids
In this talk, Dr. Alessandro Prigione will discuss how stem cells are generated from patients to derive models of the …
