A new drug offers hope for young boys with the progressive neuromuscular disease Duchenne muscular dystrophy (DMD)A genetic disorder characterized by progressive muscle degeneration and weakness due to alterations of a protein called dystrophin that keeps muscle cells intact. by potentially offering an alternative to high-dose glucocorticoids that have significant side effects. Interim results from a 24-month clinical trial at Duke Health and other institutions suggest that the drug, vamorolone, may […]
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